Challenges
EXPERT will address several major challenges that have limited mRNA therapeutics from displaying their full potential:
- The ability to achieve functional target tissue delivery of mRNA by nanomedicine design
- The capability to circumvent adverse immune responses towards mRNA nanomedicines
- The scientific knowledge to achieve general applicability of an mRNA-based platform technology for various diseases and administration routes
- The know-how to accomplish quality control and overcome regulatory hurdles
Project Objectives
- Development of off-the-shelf targeted mRNA nanomedicines
- Production of mRNA nanomedicines in a quality-by-design (QbD) approach
- Good Manufacturing Practice scale-up to be ready for clinical translation
- Investigation of mRNA nanomedicines for heart failure patients